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Publications

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Filters: Keyword is Genetic Therapy  [Clear All Filters]
2023
Hardwiring tissue-specific AAV transduction in mice through engineered receptor expression., Zengel, James, Wang Yu Xin, Seo Jai Woong, Ning Ke, Hamilton James N., Wu Bo, Raie Marina, Holbrook Colin, Su Shiqi, Clements Derek R., et al. , Nat Methods, 2023 Jul, Volume 20, Issue 7, p.1070-1081, (2023)
2018
CRISPR GENOME SURGERY IN THE RETINA IN LIGHT OF OFF-TARGETING., Cho, Galaxy Y., Schaefer Kellie A., Bassuk Alexander G., Tsang Stephen H., and Mahajan Vinit B. , Retina, 2018 08, Volume 38, Issue 8, p.1443-1455, (2018)
2016
Reprogramming metabolism by targeting sirtuin 6 attenuates retinal degeneration., Zhang, Lijuan, Du Jianhai, Justus Sally, Hsu Chun-Wei, Bonet-Ponce Luis, Wu Wen-Hsuan, Tsai Yi-Ting, Wu Wei-Pu, Jia Yading, Duong Jimmy K., et al. , J Clin Invest, 2016 Dec 01, Volume 126, Issue 12, p.4659-4673, (2016)