Calpain-5 gene expression in the mouse eye and brain
, BMC research notes, Volume 10, Number 1, p.602, (2017)
CRISPR-Cas Genome Surgery in Ophthalmology
, Translational vision science & technology, Volume 6, p.13–13, (2017)
CRISPR-Mediated Ophthalmic Genome Surgery
, Current ophthalmology reports, Volume 5, p.199–206, (2017)
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
, Lancet, 2017 Aug 26, Volume 390, Issue 10097, p.849-860, (2017)
Genome Surgery and Gene Therapy in Retinal Disorders.
, Yale J Biol Med, 2017 Dec, Volume 90, Issue 4, p.523-532, (2017)