Publications

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2017

CRISPR-Mediated Ophthalmic Genome Surgery   |   G.Y. Cho; Y. Abdulla; J.D. Sengillo; S. Justus; K.A. Schaefer; A.G. Bassuk; S.H. Tsang; V.B. Mahajan   |   Details

Genome Surgery and Gene Therapy in Retinal Disorders.   |   L. Chan; V.B. Mahajan; S.H. Tsang   |   Details
Diagnostic and Therapeutic Challenges.   |   P. Mishra; V. Kanaujia; K. Sharma; V.B. Mahajan; E.K. Chin   |   Details
Limbal Trocar-Cannulas for Complex Vitrectomy Surgery.   |   K.A. Mears; V.B. Mahajan   |   Details
Acanthamoeba Endophthalmitis After Recurrent Keratitis And Nodular Scleritis   |   Z. Mammo; D.R.P. Almeida; M.A. Cunningham; E.K. Chin; V.B. Mahajan   |   Details
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.   |   S. Russell; J. Bennett; J.A. Wellman; D.C. Chung; Z.F. Yu; A. Tillman; J. Wittes; J. Pappas; O. Elci; S. McCague; D. Cross; K.A. Marshall; J. Walshire; T.L. Kehoe; H. Reichert; M. Davis; L. Raffini; L.A. George; P. Hudson; L. Dingfield; X. Zhu; J.A. Haller; E.H. Sohn; V.B. Mahajan; W. Pfeifer; M. Weckmann; C. Johnson; D. Gewaily; A. Drack; E. Stone; K. Wachtel; F. Simonelli; B.P. Leroy; F. Wright; K.A. High; A.M. Maguire   |   Details
CRISPR-Cas Genome Surgery in Ophthalmology   |   J.E. DiCarlo; J.D. Sengillo; S. Justus; T. Cabral; S.H. Tsang; V.B. Mahajan   |   Details
Recessive coding and regulatory mutations in FBLIM1 underlie the pathogenesis of chronic recurrent multifocal osteomyelitis (CRMO).   |   A.J. Cox; B.W. Darbro; R.M. Laxer; G. Velez; X. Bing; A.L. Finer; A. Erives; V.B. Mahajan; A.G. Bassuk; P.J. Ferguson   |   Details
Gene Therapy Restores Mfrp and Corrects Axial Eye Length   |   G. Velez; S.H. Tsang; Y.T. Tsai; C.W. Hsu; A. Gore; A.H. Abdelhakim; M. Mahajan; R.H. Silverman; J.R. Sparrow; A.G. Bassuk;   |   Details
Ocular hypertension after intravitreal dexamethasone (Ozurdex) sustained-release implant   |   E.K. Chin; D.R.P. Almeida; G. Velez; K. Xu; M. Peraire; M. Corbella; Y.M. Elshatory; Y.H. Kwon; K.M. Gehrs; C. Boldt;   |   Details

2016

COMBINED VITRECTOMY AND INTRAVITREAL DEXAMETHASONE (OZURDEX) SUSTAINED-RELEASE IMPLANT.   |   A. Zheng; E.K. Chin; D.R.P. Almeida; S.H. Tsang; V.B. Mahajan   |   Details
Management of Pediatric Aphakic Glaucoma With Vitrectomy and Tube Shunts.   |   Y.M. Elshatory; E.H. Gauger; Y.H. Kwon; W.L.M. Alward; C. Boldt; S.R. Russell; V.B. Mahajan   |   Details
Secondary glaucoma in CAPN5-associated neovascular inflammatory vitreoretinopathy.   |   A. Cham; M. Bansal; H.K. Banda; Y. Kwon; P.S. Tlucek; A.G. Bassuk; S.H. Tsang; W.M. Sobol; J.C. Folk; S. Yeh; V.B. Mahajan   |   Details
Small-angle X-ray scattering of calpain-5 reveals a highly open conformation among calpains   |   L. Gakhar; A.G. Bassuk; G. Velez; S. Khan; J. Yang; S.H. Tsang; V.B. Mahajan   |   Details
Precision medicine: genetic repair of retinitis pigmentosa in patient-derived stem cells   |   A.G. Bassuk; A. Zheng; Y. Li; S.H. Tsang; V.B. Mahajan   |   Details
CRISPR Repair Reveals Causative Mutation in a Preclinical Model of Retinitis Pigmentosa.   |   W.H. Wu; Y.T. Tsai; S. Justus; T.T. Lee; L. Zhang; C.S. Lin; A.G. Bassuk; V.B. Mahajan; S.H. Tsang   |   Details
Neuroretinal hypoxic signaling in a new preclinical murine model for proliferative diabetic retinopathy.   |   K.J. Wert; V.B. Mahajan; L. Zhang; Y. Yan; Y. Li; J. Tosi; C.Wei Hsu; T. Nagasaki; K.M. Janisch; M.B. Grant; M. Mahajan; A.G. Bassuk; S.H. Tsang   |   Details

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